Injecting medicines into amniotic fluid may be a viable strategy for treating SMA before birth, according to a new study in ...

Making a situation accessible is more about mindset than things, says columnist. That's why attitude is important.

With a fresh cup of coffee balanced on my knee, I quickly scanned my church’s cafe area for a place to land where I could have a supportive tabletop. The only vacant spot at a table was next to a ...

SMA gene therapy GC101 was found to rescue disease manifestations in mice and to be safe in non-human primates.

Blood creatinine-to-cystatin-c ratio, an indicator of muscle mass and strength, may be a treatment response biomarker of SMA, ...

A wearable robotic device called HAL improved walking ability for SMA patients who also received Spinraza (nusinersen), a ...

Spoiler alert: This column discusses the plot of the 2024 film “The Substance.” Hollywood was abuzz about Coralie Fargeat’s 2024 film “The Substance” when it arrived on the scene. It was a ...