Martin Mwita, 20, is the first patient in St. Louis and among the first across the country to receive a new gene therapy for ...

As scientists explore treating genetic disorders before birth, the promise of foetal gene therapy is growing—but there are ...

Researchers at the University of Minnesota have completed a first-in-human clinical trial testing a CRISPR/Cas9 gene-editing ...

Researchers have completed a first-in-human clinical trial testing a CRISPR/Cas9 gene-editing technique to help the immune system fight advanced gastrointestinal (GI) cancers. The results show ...

Joe DePinto from McKesson discussed the challenges facing cell and gene therapies, particularly around reimbursement, and ...

An investigational gene therapy has successfully restored immune function in all nine children treated with the rare and life ...

Investing in the specialist workforce and overcoming access barriers is essential to successful delivery of this therapy in the NHS, write Jessie Enakhumhe and Yasmin Sheikh Casgevy, or exagamglogene ...

QIAcuity digital PCR kits, assays and protocols for lentivirus-based therapies support quality control in cell and gene ...

Discover six hemophilia companies developing new treatments for the genetic bleeding disorder, from gene therapies to RNAi ...

Opportunities to implement AI across the entire R&D pipeline The gene therapy development process requires engagement with a large network of partners, including large pharma, small and mid-size ...