The one-off treatment highlights the promise of a new type of gene editing and the challenges of using it to treat extremely rare genetic diseases.

After spending over 300 days at CHOP, KJ Muldoon has been released from the hospital after receiving personalized CRISPR gene ...

The personalized CRISPR treatment could be the future of gene therapy, but hurdles remain before everyone has access.

A baby born with a rare and dangerous genetic disease is growing and thriving after getting an experimental gene editing treatment made just for him.

A baby boy with a devastating genetic disease is ... Yet, the drug that it developed, described in the New England Journal of Medicine on May 15, is specific to Muldoon’s genetic sequence ...

Baby KJ Muldoon, the first patient to successfully receive personalized CRISPR gene editing therapy has returned home after over 300 days at the hospital.

The baby's disease prevented the liver from removing ... fast-tracking approval of the new therapy by the Food and Drug Administration. Scientists expedited safety testing using cell cultures ...

Experts are seeing a revival of classic and once old fashioned baby names in 2025 – with these six girl names popular among parents of today.

The baby, now nine and a half months old ... KJ’s treatment offers a new path for companies to develop personalised treatments without going through years of expensive development and testing.

The goal is to reuse key parts of the treatment and simply swap in a custom set of instructions for each patient's specific ...

A baby boy with a devastating genetic disease is ... Yet, the drug that it developed, described in the New England Journal of Medicine on 15 May, is specific to Muldoon’s genetic sequence ...