The focus should be on respecting the evidence, and our lived experiences, by providing all children with an appropriate language. Proposing gene therapies for deaf children risks overlooking the ...

The findings, published in The Lancet Oncology, hint at a new frontier in the fight against some of the deadliest forms of ...

Patients with severe dystrophic epidermolysis bullosa, or EB, have skin so fragile, the slightest touch can lead to ...

In April, the Deparment of Health and Human Services shuttered the committe that oversaw newborn screenings. Advocates hope ...

Researchers at the University of Minnesota have completed a first-in-human clinical trial testing a CRISPR/Cas9 gene-editing technique to help the immune system fight advanced gastrointestinal (GI) ...

A new gene therapy reversed heart failure in pigs by repairing heart function through cBIN1, showing major promise for future ...

Researchers have completed a first-in-human clinical trial testing a CRISPR/Cas9 gene-editing technique to help the immune system fight advanced gastrointestinal (GI) cancers. The results show ...

Researchers at the University of Minnesota have completed a first-in-human clinical trial testing a CRISPR/Cas9 gene-editing ...

As scientists explore treating genetic disorders before birth, the promise of foetal gene therapy is growing—but there are ...

SK pharmteco has opened its new Current Good Manufacturing Practice (CGMP) plasmid suite at its facility in King of Prussia, ...

Researchers from the Keck School of Medicine of USC have developed an advanced analytical tool using spectral flow cytometry to analyze CAR T cells, revealing that a five-day expansion process ...

The researchers now plan to incorporate their new tool into a drug development program, leading to early clinical trials.