A CRISPR treatment seems to have been effective for a baby’s devastating disease, but it is not clear whether such bespoke therapies can be widely applied ...

The one-off treatment highlights the promise of a new type of gene editing and the challenges of using it to treat extremely rare genetic diseases.

The personalized CRISPR treatment could be the future of gene therapy, but hurdles remain before everyone has access.

Researchers say the CRISPR-based technique used could eventually be employed to treat more people with rare genetic diseases ...

Experts are seeing a revival of classic and once old fashioned baby names in 2025 – with these six girl names popular among parents of today.

A baby born with a rare and dangerous genetic disease is growing and thriving after getting an experimental gene editing treatment made just for him.

You may have seen it in the news recently: a baby in Pennsylvania with a rare genetic disorder was healed with a personalized ...

Breakthrough therapy may pave the way for personalized cures and a cheaper path to treating ultra-rare conditions.

The baby's disease prevented the liver from removing ... fast-tracking approval of the new therapy by the Food and Drug Administration. Scientists expedited safety testing using cell cultures ...

A baby born with a rare genetic disease is "growing ... published the results of their work in the New England Journal of Medicine. Gene therapy is an innovative treatment that aims to cure ...