Spacecraft unveils 1st-ever images of sun's south pole: 'Beginning of a new era' ...

The NHS in England will be the first health system in the world to roll-out a ‘trojan horse’ targeted therapy for blood cancer patients which could halt the disease’s progression by nearly three times ...

The FDA’s accelerated approval pathway plays a vital role, and scrapping it or reversing course on already-approved therapies ...

Participants with Duchenne muscular dystrophy (DMD) who received RGX-202 demonstrated functional improvement and better ...

Ocugen, Inc. (NASDAQ: OCGN) announced its participation in the 2025 BIO International Convention, held from June 16-19 at the ...

According to a new study in Haemophilia, up to 60% of patients with severe HA have no known family history, making early ...

A combination therapy that adds a recently approved drug to the current standard of care for newly diagnosed acute myeloid ...

A gene transfer approach to treating the bleeding disorder hemophilia B remains safe and effective long-term, as scientists ...

Subsequent studies by other investigators confirmed those early results, ultimately leading to the FDA approval of ...

The benefits of drug warranties extend beyond risk management. They can also serve as market differentiators in crowded ...

The firm expects to complete enrolling the REVEAL trial, in which patients will receive the ASO, dubbed ION582, in 2026.