When even one tiny section of a person’s genetic code becomes mutated or modified, cells can begin to act out of ...

An investigational gene therapy has successfully restored immune function in all nine children treated with the rare and life ...

Martin Mwita, 20, is the first patient in St. Louis and among the first across the country to receive a new gene therapy for ...

The Global Cell And Gene Therapy Market is valued at USD 20.5 Billion in 2024 and is projected to reach a value of USD 128.8 ...

The first patient to receive a new gene therapy at the Children's Hospital of Philadelphia is now living pain-free for the ...

Liver damage related to Zolgensma gene therapy usually resolves within a few months of treatment, a study found.

Multidisciplinary coordination across prescribing teams, nursing, laboratory medicine, finance, and infusion centers is ...

Joe DePinto from McKesson discussed the challenges facing cell and gene therapies, particularly around reimbursement, and ...

The U.S. Food and Drug Administration approved Abeona Therapeutics' gene therapy for a rare skin disorder on Tuesday.

A new study in Human Gene Therapy describes a machine learning (ML) model that can be used as a surrogate for laborious in ...

Investing in the specialist workforce and overcoming access barriers is essential to successful delivery of this therapy in the NHS, write Jessie Enakhumhe and Yasmin Sheikh Casgevy, or exagamglogene ...