Sickle cell disease affects around 100,000 people in the US, most commonly African Americans. It leads to anemia, vaso-occlusive ... that deform the cell. The CRISPR/Cas9 therapy approved today ...

A colorized image from a scanning electron microscopic shows the differences between healthy red blood cells and one, left, from an 18-year-old patient with sickle cell anemia. (Janice Hanley Carr ...

is a first-of-its-kind treatment that uses the powerful gene-editing tool Crispr to target the underlying cause of sickle cell. Sickle cell disease, also called sickle cell anemia, is a group of ...

‘A revolutionary step in treating #sickle_cell_disease! #CRISPR gene editing is being ... causing blockages, anemia, pain, organ failure, and a significantly shortened lifespan.

Gene therapy has always held enormous promise to correct genetic diseases, but turning that potential into treatments has ...

Voxelotor (Oxbryta) can help with anemia. Blood transfusions Stem cell transplants might cure the disease for some children and teenagers. CRISPR gene editing for sickle cell disease In December ...

CRISPR, or clustered regularly interspaced ... With sickle cell disease — also called sickle cell anemia — red blood cells take on a folded or sickle shape that can clog tiny blood vessels ...

Sickle cell anemia is a painful ... Recent advances in what's known as CRISPR gene-editing technology helps correct the disorder by tweaking the underlying gene abnormality behind it.

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In hospitals, doctors would treat the anemia with blood ... approved gene therapies for sickle cell disease. Called Casgevy, the treatment was developed by CRISPR Therapeutics and Vertex ...

A big breakthrough is being hailed in the world of gene editing, with the first custom-designed treatment using CRISPR technology.